Researchers design potential therapy for children with rare genetic conditions

A research team has identified new potential treatments for children with rare genetic conditions of blood vessels, which cause severe, lifelong, and disabling symptoms like seizures and impaired development. The researchers – at the Francis Crick Institute and Great Ormond Street Hospital (GOSH)/UCL Great Ormond Street Institute of Child Health – showed that problems with … Continue reading Researchers design potential therapy for children with rare genetic conditions